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Bethesda North Marriott Hotel and Conference Center

Oct 25, 2017 7:00 AM - Oct 27, 2017 3:00 PM

5701 Marinelli Road, , North Bethesda, MD 20852 , USA

DIA/FDA Oligonucleotide-Based Therapeutics Conference

Convening industry and health authorities to inform, educate, and share advancements in oligonucleotide-based therapeutic product development.

Session 3A: Starting Materials: Beyond Simple DNA and RNA Derived Phosphoramidites

Session Chair(s)

Fran  Wincott, PhD

Fran Wincott, PhD

President

Wincott & Associates, LLC, United States

There has been a dramatic increase in the complexity of drug candidates being promoted into preclinical and clinical development. These oligonucleotides often have significant chemical modifications requiring specialty starting materials. Furthermore, recent communications from regulatory authorities regarding the selection and justification of starting materials have been issued. This session will address the general starting material principles outlined in Q11 and the accompanying Q&A document. In addition, strategies for defining and sourcing non-standard oligonucleotide-specific starting materials will be presented. The presentations will be followed by a 30 minute panel discussion.

Learning Objective :
  • Understand the general principles discussed in Q11 as they apply to the selection and justification of starting materials
  • Explain the unique challenges associated with starting material selection for oligonucleotides
  • Speaker(s)

    Timothy  Watson, PhD

    Identification of Starting Materials for Oligonucleotides by Applying ICH Q11

    Timothy Watson, PhD

    Gilead Sciences, United States

    Vice President- Head of CMC Regulatory Affairs

    Christoph  Rosenbohm, PhD, MBA

    Integrating LNA Phosphoramidites into the Regular Supply Chain

    Christoph Rosenbohm, PhD, MBA

    Roche Innovation Center Copenhagen, Denmark

    Vice President, Head of Discovery Operations

    Lubo  Nechev, PhD

    GalNAc Solid Support as Starting Material for Oligonucleotide Manufacturing

    Lubo Nechev, PhD

    Alnylam Pharmaceuticals, United States

    Chief CMC Officer

      Panel Discussion

    Panel Discussion

    All Session Speakers, United States

    Olen M. Stephens, PhD

    Panelist

    Olen M. Stephens, PhD

    FDA, United States

    Chemist Reviewer, CMC Reviewer, CDER/OPQ/ONDP

    René  Thürmer, PhD

    Panelist

    René Thürmer, PhD

    Federal Institute for Drugs and Medical Devices, Germany

    Quality Assessor

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